Abstract
Gene therapy has emerged as a transformative approach in the development of novel therapeutic strategies for a range of genetic and acquired diseases. By delivering functional genes to correct defective ones, gene therapy offers long-lasting and potentially curative treatments. Recent technological advances, including CRISPR-Cas9, viral vector engineering, and non-viral delivery systems, have significantly enhanced the precision and safety of gene delivery. This article examines the current state and future potential of gene therapy in drug development, addressing applications, regulatory challenges, and ethical considerations.
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