Abstract
Gene therapy represents a promising frontier in the treatment of genetic disorders, cancers, and other chronic diseases by correcting defective genes. Recent advancements have improved the efficiency and safety of gene delivery systems, overcoming many challenges previously associated with this therapeutic approach. This article reviews the recent progress in gene therapy, focusing on viral and non-viral delivery systems, gene editing techniques like CRISPR-Cas9, and current clinical applications. Additionally, it highlights the future prospects and challenges, including the potential for personalized gene therapies and the integration of gene therapy with other emerging technologies.
All articles published in the American Journal of Pharmaceutics are open access and licensed under the Creative Commons Attribution 4.0 International License (CC BY 4.0). This license allows users to:
-
Share — copy and redistribute the material in any medium or format
-
Adapt — remix, transform, and build upon the material for any purpose, even commercially
Under the following terms:
-
Attribution — Appropriate credit must be given, a link to the license must be provided, and any changes must be indicated.
-
Authors retain full copyright of their work.
-
The journal does not restrict reuse of content, provided proper citation of the original publication is made.